Six new medicines approved including first treatment for rare heart condition
Six new medicines have been approved for use in Scotland, including the first treatment for a rare "potentially life-threatening" heart condition.
The Scottish Medicines Consortium (SMC) has approved Tafamidis for the treatment of a rare heart condition called amyloidosis cardiomyopathy (ATTR-CM).
It is the first treatment to be licensed to treat wild-type or hereditary amyloidosis cardiomyopathy and Scotland is the first in the UK to make this medicine routinely available on the NHS, pharmaceutical company Pfizer said.
ATTR-CM is a rare condition where abnormal proteins called amyloid build up in tissues around the heart.
Dr Caroline Coats, consultant cardiologist at NHS Greater Glasgow and Clyde, said: "Transthyretin amyloid cardiomyopathy is a rare, under-diagnosed and potentially life-threatening condition, for which there is a significant unmet medical need.
"This decision is a welcome step to help expand treatment options for patients."
Owen Marks, head of rare diseases, Pfizer UK added: "This decision is an important milestone for eligible patients in Scotland, who until now have not had a specific treatment option for amyloidosis cardiomyopathy.
"We'll continue to work to help improve the care and diagnosis of ATTR-CM in Scotland and in the rest of the UK."
The SMC has also approved the use of selpercatinib on an interim basis to treat a rare type of non-small cell lung cancer.
It will be available to patients while further research is undertaken.
The SMC will review the evidence and make a decision on routine availability in NHS Scotland.
Durvalumab was approved for use to treat adults with advanced biliary tract cancer, which is cancer of the bile ducts that carry bile from the liver and the gallbladder to the intestines, which is newly diagnosed.
Avacopan was accepted for the treatment of adults with rare conditions that can cause blood vessels to become inflamed which can restrict blood flow and cause damage to vital organs.
Bimekizumab was accepted for the treatment of adults with psoriatic arthritis, an inflammatory arthritis associated with the skin condition psoriasis.
Risankizumab was accepted for treating Crohn's disease in patients aged 16 or older.
However, some medicines were not accepted for use.
The committee was unable to accept efgartigimod alfa for the treatment of adult patients with the muscle weakness condition generalised Myasthenia Gravis (gMG).
It was also unable to accept pegunigalsidase alfa for the treatment of Fabry disease, a rare inherited condition that can lead to kidney failure and heart problems.
Mercaptamine was also not accepted for use in patients with nephropathic cystinosis, a rare inherited condition that can affect the kidneys.
Reference: Sky News:
No thoughts on “Six new medicines approved including first treatment for rare heart condition”
Articles - Most Read
- LIVER DIS-EASE AND GALL BLADDER DIS-EASE
- African Wholistics - Medicines, Machines and Ignorance
- African Holistics - Seduced by Ignorance and Research
- African Wholistics -The Overlooked Revolution
- The Children of the Sun-3
- Kidney Stones-African Holistic Health
- PART ONE: DIS-EASE TREATMENT AND HEALTH-3
- 'Tortured' and shackled pupils freed from Nigerian Islamic school
- PART ONE: DIS-EASE TREATMENT AND HEALTH-2
- The Serpent and the RainBow-The Jaguar - 2
- PART ONE: DIS-EASE TREATMENT AND HEALTH-4
- PART ONE: DIS-EASE TREATMENT AND HEALTH-5
- King Leopold's Ghost - Introduction
- African Wholistics - Medicine
- PART ONE: DIS-EASE TREATMENT AND HEALTH-6
- The Mystery System
- The Black Pharaohs Nubian Pharaohs of Ancient Egypt
Who's On Line?
We have 13 guests and no members online
Ad Agency Remote
Articles - Latest
- Everything you need to know about mangosteen
- Should I worry about my clicking joints – and stop cracking my knuckles?
- The Children Of the Sun-Asia-4
- THE HEALTH BENEFITS OF MUSTARD
- Prickly heat - expert shares four signs you have heat rash and how to treat it
- Suffering with eye eczema? Experts reveal how to treat the symptoms
- Peanut Butter Nutrition Facts and Health Benefits
- Hypertension - High Blood Pressure - Stress
- What Is Spelt, and Is It Good for You?
- Groundbreaking treatment helps repair vision after eye injury
- The Benefits of Eating Groats
- Five signs when walking that could indicate Lewy body dementia - seek medical help
- What Are Chickpeas and Are They Healthy?
- Six new medicines approved including first treatment for rare heart condition
- Peanuts 101: Nutrition Facts and Health Benefits
- What is mouth and oropharyngeal cancer?
- Certain fruits eaten an 'hour' before bed may 'significantly increase' sleep efficiency
- Scientists sequence Beethoven’s genome using locks of his hair
- Lemongrass: Expert opinions and healthy portions